In the first preprint from my and @grunewald.bsky.social labs @TU_Muenchen, we show how this could work for new #celltherapies and #genetherapies. (2)
November 26, 2024 at 1:36 PM
In the first preprint from my and @grunewald.bsky.social labs @TU_Muenchen, we show how this could work for new #celltherapies and #genetherapies. (2)
Secure your spot! Join our webinar on July 30 with Dr. Rebecca Ahrens-Nicklas to learn about advances in genomic therapies for severe metabolic diseases. spkl.io/63328AElxj #RareDiseases #GeneTherapies
July 23, 2025 at 12:00 PM
Secure your spot! Join our webinar on July 30 with Dr. Rebecca Ahrens-Nicklas to learn about advances in genomic therapies for severe metabolic diseases. spkl.io/63328AElxj #RareDiseases #GeneTherapies
A new study helps researchers engineer better gene therapies. bit.ly/4jhW2Pw #GeneTherapies #BCMResearch
New study helps researchers engineer better gene therapies
This study will make basic research on AAV vectors for gene delivery and preclinical gene therapy studies in mice more efficient and reproducible.
bit.ly
April 1, 2025 at 8:50 PM
A new study helps researchers engineer better gene therapies. bit.ly/4jhW2Pw #GeneTherapies #BCMResearch
A question on #GeneTherapies #FeesAndCharges tabled by Nickie Aiken on 19-12-2023 has been answered by Andrew Stephenson. https://questions-statements.parliament.uk/written-questions/detail/2023-12-19/7672
January 8, 2024 at 11:11 AM
A question on #GeneTherapies #FeesAndCharges tabled by Nickie Aiken on 19-12-2023 has been answered by Andrew Stephenson. https://questions-statements.parliament.uk/written-questions/detail/2023-12-19/7672
Going to #ASH24 this looks like a great session for #celltherapies and #biomanufacturing looking forward to seeing the new #genetherapies
Thank you to Dr. Marcela Maus for previewing the Therapeutic #GeneEditing of #StemCells in #ClassicalHematology and #MalignantHematology session at #ASH24!
#ASHinaFlash brings you micro doses of exciting #hematology breakthroughs!
#HemeOnc #HemeSky #HemeSky
www.youtube.com/watch?v=A6Mx...
#ASHinaFlash brings you micro doses of exciting #hematology breakthroughs!
#HemeOnc #HemeSky #HemeSky
www.youtube.com/watch?v=A6Mx...
ASH in a Flash - Therapeutic Gene Editing of Stem Cells in Classical & Malignant Hematology
YouTube video by American Society of Hematology
www.youtube.com
December 4, 2024 at 1:00 PM
Going to #ASH24 this looks like a great session for #celltherapies and #biomanufacturing looking forward to seeing the new #genetherapies
From March 12-13 at Empowering Patients 2025, we'll explore:
✔️The Value of Patients + Advocates
✔️Why Are Clinical Trials for #RareDiseases Different?
✔️Developing #GeneTherapies as Platform Technologies
Register for FREE! #ASGCTAdvocacy #PatientEducation www.asgct.org/events/empow...
December 9, 2024 at 5:53 PM
From March 12-13 at Empowering Patients 2025, we'll explore:
✔️The Value of Patients + Advocates
✔️Why Are Clinical Trials for #RareDiseases Different?
✔️Developing #GeneTherapies as Platform Technologies
Register for FREE! #ASGCTAdvocacy #PatientEducation www.asgct.org/events/empow...
#Observationalstudies #interventionaltrials #celltherapies #genetherapies #AI #clinicaltrials #integratedendtoendtrials #DCTmodels #interventionaltrialdesigns #digitaltechnologies #patientparticipation #virtualobservationalstudies #hybridobservationalstudies
pharmaphorum.com/patients/uni...
pharmaphorum.com/patients/uni...
Unifying observational research with a next-generation virtual approach
Explore the unification of observational research with a next-generation virtual approach in decentralised clinical trials (DCTs). Learn more about the benefits and advancements in this innovative met...
pharmaphorum.com
April 4, 2025 at 9:31 AM
From #GLP1 agonists to #GeneTherapies, innovative drug therapies are revolutionizing #diabetes management. Explore the future of #personalizedmedicine now!
Read full article 👉 bio-integration.org/novel-diabet...
#DiabetesResearch #biotech #precisionmedicine
Read full article 👉 bio-integration.org/novel-diabet...
#DiabetesResearch #biotech #precisionmedicine
Unlocking the Potential of Receptor-Based Approaches in Diabetes Treatment
Announcing a new article publication for BIO Integration journal. Diabetes, a common metabolic condition, poses a substantial health burden worldwide. To revolutionize diabetes management, enhance g...
bio-integration.org
February 10, 2025 at 9:35 AM
From #GLP1 agonists to #GeneTherapies, innovative drug therapies are revolutionizing #diabetes management. Explore the future of #personalizedmedicine now!
Read full article 👉 bio-integration.org/novel-diabet...
#DiabetesResearch #biotech #precisionmedicine
Read full article 👉 bio-integration.org/novel-diabet...
#DiabetesResearch #biotech #precisionmedicine
A question on #GeneTherapies tabled by Baroness Ritchie of Downpatrick on 29-10-2024 has been answered by Baroness Merron. https://questions-statements.parliament.uk/written-questions/detail/2024-10-29/HL2124
November 7, 2024 at 4:41 PM
A question on #GeneTherapies tabled by Baroness Ritchie of Downpatrick on 29-10-2024 has been answered by Baroness Merron. https://questions-statements.parliament.uk/written-questions/detail/2024-10-29/HL2124
A question on #RareCancers #GeneTherapies tabled by Brian Mathew on 05-03-2025 has been answered by Ashley Dalton. https://questions-statements.parliament.uk/written-questions/detail/2025-03-05/35930
March 13, 2025 at 6:20 PM
A question on #RareCancers #GeneTherapies tabled by Brian Mathew on 05-03-2025 has been answered by Ashley Dalton. https://questions-statements.parliament.uk/written-questions/detail/2025-03-05/35930
This #RetinitisPigmentosa Month, we’re spotlighting Sam Malka’s research on improving diagnosis for Black African communities. Her discovery of a genetic change opens the door to future #GeneTherapies.
Find out more: buff.ly/3CHwgV8
@ucleye.bsky.social #GenomicsEngland
Find out more: buff.ly/3CHwgV8
@ucleye.bsky.social #GenomicsEngland
February 11, 2025 at 12:08 PM
This #RetinitisPigmentosa Month, we’re spotlighting Sam Malka’s research on improving diagnosis for Black African communities. Her discovery of a genetic change opens the door to future #GeneTherapies.
Find out more: buff.ly/3CHwgV8
@ucleye.bsky.social #GenomicsEngland
Find out more: buff.ly/3CHwgV8
@ucleye.bsky.social #GenomicsEngland
A question on #GeneTherapies #Innovation tabled by Jim Shannon on 07-02-2024 has been answered by Andrea Leadsom. https://questions-statements.parliament.uk/written-questions/detail/2024-02-07/13579
February 20, 2024 at 12:03 PM
A question on #GeneTherapies #Innovation tabled by Jim Shannon on 07-02-2024 has been answered by Andrea Leadsom. https://questions-statements.parliament.uk/written-questions/detail/2024-02-07/13579
📢 Huge News! 📢
The MRC has launched two centres of research excellence to transform gene therapies: IDRM’s Paul Riley will co-direct the MRC/BHF CoRE in Advanced Cardiac Therapies & Stephan Sanders will direct the MRC CoRE in Therapeutic Genomics.
Read more: lnkd.in/g-3CmAsP
#GeneTherapies
The MRC has launched two centres of research excellence to transform gene therapies: IDRM’s Paul Riley will co-direct the MRC/BHF CoRE in Advanced Cardiac Therapies & Stephan Sanders will direct the MRC CoRE in Therapeutic Genomics.
Read more: lnkd.in/g-3CmAsP
#GeneTherapies
December 11, 2024 at 10:40 AM
📢 Huge News! 📢
The MRC has launched two centres of research excellence to transform gene therapies: IDRM’s Paul Riley will co-direct the MRC/BHF CoRE in Advanced Cardiac Therapies & Stephan Sanders will direct the MRC CoRE in Therapeutic Genomics.
Read more: lnkd.in/g-3CmAsP
#GeneTherapies
The MRC has launched two centres of research excellence to transform gene therapies: IDRM’s Paul Riley will co-direct the MRC/BHF CoRE in Advanced Cardiac Therapies & Stephan Sanders will direct the MRC CoRE in Therapeutic Genomics.
Read more: lnkd.in/g-3CmAsP
#GeneTherapies
We're on Bluesky! Follow us for exciting updates, insights, and arising opportunities as we harness #engineeringbiology for safe and effective #genetherapies.
Join our upcoming @ukri.org - hosted webinar to learn more
📅 Date: Monday 9th June 2025
⏰ Time: 1-2pm UK time
🔗 edin.ac/43O5PIC
Join our upcoming @ukri.org - hosted webinar to learn more
📅 Date: Monday 9th June 2025
⏰ Time: 1-2pm UK time
🔗 edin.ac/43O5PIC
Engineering Biology Mission Hubs showcase: advanced therapeutics
Join members from the team leading the Engineered Genetic Control Systems for Advanced Therapeutics Mission Hub as they provide an overview of their expansive engineering biology programme.
edin.ac
April 10, 2025 at 9:57 AM
We're on Bluesky! Follow us for exciting updates, insights, and arising opportunities as we harness #engineeringbiology for safe and effective #genetherapies.
Join our upcoming @ukri.org - hosted webinar to learn more
📅 Date: Monday 9th June 2025
⏰ Time: 1-2pm UK time
🔗 edin.ac/43O5PIC
Join our upcoming @ukri.org - hosted webinar to learn more
📅 Date: Monday 9th June 2025
⏰ Time: 1-2pm UK time
🔗 edin.ac/43O5PIC
Deadline is today for abstracts for talks for our GRC Cilia, Mucus & Mucociliary Interactions in Pomona, California 16-21/02/25! Organized by myself, Katharina Ribbeck, Marcus Mall & Sudipto Roy! #cilia #biophysics #RareDisease #biofilms #GeneTherapies #Mucus #PCD #CF
www.grc.org/cilia-mucus-...
www.grc.org/cilia-mucus-...
November 25, 2024 at 8:34 AM
Deadline is today for abstracts for talks for our GRC Cilia, Mucus & Mucociliary Interactions in Pomona, California 16-21/02/25! Organized by myself, Katharina Ribbeck, Marcus Mall & Sudipto Roy! #cilia #biophysics #RareDisease #biofilms #GeneTherapies #Mucus #PCD #CF
www.grc.org/cilia-mucus-...
www.grc.org/cilia-mucus-...
Discover how we harness #engineeringbiology for safe and effective #genetherapies. Sign up to our upcoming webinar.
📅 Date: Monday, 9th June 2025
⏰ Time: 1pm-2pm UK time
👉 Register here: edin.ac/43O5PIC
Kindly hosted by @ukri.org showcasing our #AdvancedTherapeutics hub.
📅 Date: Monday, 9th June 2025
⏰ Time: 1pm-2pm UK time
👉 Register here: edin.ac/43O5PIC
Kindly hosted by @ukri.org showcasing our #AdvancedTherapeutics hub.
Engineering Biology Mission Hubs showcase: advanced therapeutics
Join members from the team leading the Engineered Genetic Control Systems for Advanced Therapeutics Mission Hub as they provide an overview of their expansive engineering biology programme.
edin.ac
May 30, 2025 at 2:50 PM
Discover how we harness #engineeringbiology for safe and effective #genetherapies. Sign up to our upcoming webinar.
📅 Date: Monday, 9th June 2025
⏰ Time: 1pm-2pm UK time
👉 Register here: edin.ac/43O5PIC
Kindly hosted by @ukri.org showcasing our #AdvancedTherapeutics hub.
📅 Date: Monday, 9th June 2025
⏰ Time: 1pm-2pm UK time
👉 Register here: edin.ac/43O5PIC
Kindly hosted by @ukri.org showcasing our #AdvancedTherapeutics hub.
After years of delay, Novartis’ intrathecal Zolgensma hit its phase 3 goal, improving motor function in SMA Type 2 (ages 2–18).
Novartis paid billions for AveXis—delays highlight the complexity of gene therapies.
Hopefully, this positive news drives more investment in the space #genetherapies
Novartis paid billions for AveXis—delays highlight the complexity of gene therapies.
Hopefully, this positive news drives more investment in the space #genetherapies
January 6, 2025 at 1:40 PM
After years of delay, Novartis’ intrathecal Zolgensma hit its phase 3 goal, improving motor function in SMA Type 2 (ages 2–18).
Novartis paid billions for AveXis—delays highlight the complexity of gene therapies.
Hopefully, this positive news drives more investment in the space #genetherapies
Novartis paid billions for AveXis—delays highlight the complexity of gene therapies.
Hopefully, this positive news drives more investment in the space #genetherapies
Mark your calendar! July 30, 2025, 12-1 PM EST — webinar on platform-based therapies for inborn errors of metabolism. Featuring Dr. Rebecca Ahrens-Nicklas spkl.io/63320AEmKi
#RareDiseases #GeneTherapies
#RareDiseases #GeneTherapies
July 24, 2025 at 11:00 AM
Mark your calendar! July 30, 2025, 12-1 PM EST — webinar on platform-based therapies for inborn errors of metabolism. Featuring Dr. Rebecca Ahrens-Nicklas spkl.io/63320AEmKi
#RareDiseases #GeneTherapies
#RareDiseases #GeneTherapies
🚀 #IT delivery💉bypasses the #BBB, sending #ASOs 🧬, #GeneTherapies 🧑🔬, #Antibodies 🛡️ & #StemCells 🌱 straight into the #Brain! A lifeline for #NDDs? @mdpiopenaccess.bsky.social #NeuroTech #BrainResearch
👉 doi.org/10.3390/biom...
👉 doi.org/10.3390/biom...
September 25, 2025 at 5:27 AM
🚀 #IT delivery💉bypasses the #BBB, sending #ASOs 🧬, #GeneTherapies 🧑🔬, #Antibodies 🛡️ & #StemCells 🌱 straight into the #Brain! A lifeline for #NDDs? @mdpiopenaccess.bsky.social #NeuroTech #BrainResearch
👉 doi.org/10.3390/biom...
👉 doi.org/10.3390/biom...
On #WorldCancerDay, we acknowledge the stories behind every cancer diagnosis—resilience, loss, hope, and healing. These stories drive us to develop intelligent #GeneCircuits for next-gen cell and #genetherapies, aiming to transform outcomes for cancer patients. #UnitedByUnique
February 4, 2025 at 1:59 PM
On #WorldCancerDay, we acknowledge the stories behind every cancer diagnosis—resilience, loss, hope, and healing. These stories drive us to develop intelligent #GeneCircuits for next-gen cell and #genetherapies, aiming to transform outcomes for cancer patients. #UnitedByUnique
This is just a first small step for #AI in #PrecisionMedicine. We’re working on many more AI-guided CAR-T cell approaches and hope that #GenerativeAI can democratize and greatly accelerate binder design for new #celltherapies and #genetherapies, especially in the context of cancer resistance. (7)
November 26, 2024 at 2:07 PM
This is just a first small step for #AI in #PrecisionMedicine. We’re working on many more AI-guided CAR-T cell approaches and hope that #GenerativeAI can democratize and greatly accelerate binder design for new #celltherapies and #genetherapies, especially in the context of cancer resistance. (7)
Kick-off of the #GeneH project in Coimbra, Portugal. A new European Project by a consortium involving Academia, Industry, Government Agencies and Patient Organizations focused on #GeneTherapies for #RareDiseases. Stay tuned to learn more
#research #innovation
#research #innovation
March 21, 2025 at 3:33 PM
Kick-off of the #GeneH project in Coimbra, Portugal. A new European Project by a consortium involving Academia, Industry, Government Agencies and Patient Organizations focused on #GeneTherapies for #RareDiseases. Stay tuned to learn more
#research #innovation
#research #innovation
Gene therapy trial gives deaf children hearing in both ears;
Study participants born unable to hear could locate sound sources, recognise speech and dance to music after treatment
www.theguardian.com/science/arti...
#science #news #biology #deafness #GeneTherapies #genetics #breakthrough
Study participants born unable to hear could locate sound sources, recognise speech and dance to music after treatment
www.theguardian.com/science/arti...
#science #news #biology #deafness #GeneTherapies #genetics #breakthrough
Gene therapy trial gives deaf children hearing in both ears
Study participants born unable to hear could locate sound sources, recognise speech and dance to music after treatment
www.theguardian.com
June 5, 2024 at 1:52 PM
Gene therapy trial gives deaf children hearing in both ears;
Study participants born unable to hear could locate sound sources, recognise speech and dance to music after treatment
www.theguardian.com/science/arti...
#science #news #biology #deafness #GeneTherapies #genetics #breakthrough
Study participants born unable to hear could locate sound sources, recognise speech and dance to music after treatment
www.theguardian.com/science/arti...
#science #news #biology #deafness #GeneTherapies #genetics #breakthrough
#advancedtherapyclinicaltrials #CellandGeneTherapyCatapult #CGTCatapult #UKtrials #UK #clinicaltrials #phaseItrials #AdvancedTherapyMedicinalProductClinicalTrialsDatabase #ATMPClinicalTrialsDatabase #globaltrials #Europeantrials #Genetherapies #ATMPclinicaltrials
pharmatimes.com/news/uk-sees...
pharmatimes.com/news/uk-sees...
UK sees 70% increase in phase I advanced therapy clinical trials in 2024 - PharmaTimes
Cell and Gene Therapy Catapult reveals significant growth in UK trials
pharmatimes.com
January 21, 2025 at 10:34 AM
Attending #SynBioBeta2025!
Our Hub focusses on #engineeringbiology for safe and effective #genetherapies. We are looking forward to insights from the Engineered Human Therapies track, connecting with industry leaders, and exploring new opportunities.
Reach out if you’d like to connect there!
Our Hub focusses on #engineeringbiology for safe and effective #genetherapies. We are looking forward to insights from the Engineered Human Therapies track, connecting with industry leaders, and exploring new opportunities.
Reach out if you’d like to connect there!
April 25, 2025 at 4:29 PM
Attending #SynBioBeta2025!
Our Hub focusses on #engineeringbiology for safe and effective #genetherapies. We are looking forward to insights from the Engineered Human Therapies track, connecting with industry leaders, and exploring new opportunities.
Reach out if you’d like to connect there!
Our Hub focusses on #engineeringbiology for safe and effective #genetherapies. We are looking forward to insights from the Engineered Human Therapies track, connecting with industry leaders, and exploring new opportunities.
Reach out if you’d like to connect there!