thermalpr.com
www.nytimes.com/2025/05/15/h...
TIME
time.com/7285695/firs...
WIRED
www.wired.com/story/a-baby...
NPR
www.npr.org/sections/sho...
The Washington Post
www.washingtonpost.com/science/2025...
Endpoints News
endpts.com/philadelphia...
STAT
www.statnews.com/2025/05/15/c...
www.nytimes.com/2025/05/15/h...
TIME
time.com/7285695/firs...
WIRED
www.wired.com/story/a-baby...
NPR
www.npr.org/sections/sho...
The Washington Post
www.washingtonpost.com/science/2025...
Endpoints News
endpts.com/philadelphia...
STAT
www.statnews.com/2025/05/15/c...
📺 The IGI’s announcement innovativegenomics.org/news/first-p... and video about CRISPR on-demand, a first in the history of medicine www.youtube.com/watch?v=H7pj...
📺 CHOP's announcement page with videos www.chop.edu/centers-prog...
📺 The IGI’s announcement innovativegenomics.org/news/first-p... and video about CRISPR on-demand, a first in the history of medicine www.youtube.com/watch?v=H7pj...
📺 CHOP's announcement page with videos www.chop.edu/centers-prog...
The patient, KJ, was born with CPS1 deficiency, a rare and severe metabolic disease affecting 1 in 1.3 million newborns. In just 6 months, scientists and doctors designed a CRISPR treatment that specifically targeted a genetic mutation in KJ’s liver cells.
The patient, KJ, was born with CPS1 deficiency, a rare and severe metabolic disease affecting 1 in 1.3 million newborns. In just 6 months, scientists and doctors designed a CRISPR treatment that specifically targeted a genetic mutation in KJ’s liver cells.
- This was medically vital, developed as a Manhattan Project for genetic medicine.
- It’s an N-of-1 therapy, a proof of concept showing how scientists can unite around a patient in need.
- It affirms the goal: Create scalable on-demand personalized CRISPR therapies accessible to all patients.
- This was medically vital, developed as a Manhattan Project for genetic medicine.
- It’s an N-of-1 therapy, a proof of concept showing how scientists can unite around a patient in need.
- It affirms the goal: Create scalable on-demand personalized CRISPR therapies accessible to all patients.